Status | Study |
Enrolling by invitation |
Study Name: SCID Bu/Flu/ATG Study With T Cell Depletion Condition: Severe Combined Immunodeficiency Date: 2012-10-19 Interventions: Biological: unrelated BM with T cell depletion |
Recruiting |
Study Name: Patients Treated for SCID (1968-2010) Condition: SCID ADA-SCID XSCID Leak Date: 2011-04-29 |
Recruiting |
Study Name: Natural History Study of SCID Disorders Condition: SCID Leaky SCID Omenn Syndrome Date: 2010-08-20 |
Terminated |
Study Name: Hematopoietic Stem Cell Transplantation (HSCT) for Children With SCID Utilizing Alemtuzumab, Plerixafor & Filgrastim Condition: Severe Combined Immunodeficiency Date: 2010-08-09 Interventions: Drug: Transplant Conditioning with Mobilization Only |
Completed |
Study Name: Pharmacokinetics and Safety Study of Single and Multiple Oral Doses Prodarsan™ in Patients With Cockayne Syndrome Condition: Cockayne Syndrome Date: 2010-05-20 Interventions: Drug: Prodarsan Prodarsan TID, oral solution, 6-8 days |
Completed |
Study Name: Pilot Study of Etanercept (Enbrel) in Children With Fanconi Anemia Condition: Fanconi Anemia Date: 2009-08-24 Interventions: Drug: Etanercept All qualified subjects receive 24 weekly subcutaneous injections of Etanercept. |
Terminated |
Study Name: rAd-p53 Gene Therapy for Advanced Oral and Maxillofacial Malignant Tumors Condition: Advanced Oral and Maxillofacial Malignant Tumors Date: 2009-05-11 Interventions: Drug: p53 gene with surgery pr |
Recruiting |
Study Name: p53 Gene Therapy for Head and Neck Malignant Tumors in Advanced Stage Condition: Neoplasms Date: 2009-05-04 Interventions: Drug: chemotherapy plus p53 ch |
Completed |
Study Name: MND-ADA Transduction of CD34+ Cells From Children With ADA-SCID Condition: Severe Combined Immunodeficiency Date: 2008-11-19 Interventions: Biological: ADA gene transfer Autologous CD34+ cells transduced with the retroviral vector MND-ADA, carr |
Completed |
Study Name: Gene Therapy for ADA-SCID Condition: Severe Combined Immunodeficiency Syndrome Date: 2008-01-08 Interventions: Genetic: gene transduced PBL and/or gene transduced HSC infusions of autologous PBL and/or HSC transduce |